September 25, 2025 9:07 AM
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Experimental Gene Therapy AMT-130 Slows Huntington’s Disease Progression by 75% in Pivotal Phase 1/2 Study
An experimental gene therapy has been found to slow the progression of Huntington’s disease in a “pivotal” Phase 1/2 study, according to the drugmaker, marking a major step toward a potential first genetic treatment for the condition. The Amsterdam-based company announced yesterday that pa...